Risdiplam (RG7916, RO7034067; Evrysdi) is a novel, potent, orally bioactive and centrally and peripherally distributed gene splicing modulator (neuromuscular disease) approved to treat spinal muscular atrophy. Risdiplam increases survival motor neuron (SMN) protein levels.
纯度:≥98%
CAS:1825352-65-5